Hear community perspectives on topics ranging from navigating a diagnosis to reflecting on clinical trial experiences.
We love aquatic therapy and we love Swim Angelfish, a swim therapy program in our area. Our 4 year old son, Ned, has been a devoted "swimmer" for nearly 2 years. Not only is swimming wonderful exercise and a meaningful confidence builder, the angelfish team is exceptional.
Cure Rare Disease, in partnership with Charles River Laboratories, has successfully created 3 mouse models that harbor the humanized form of the dystrophin gene. Each model has a mutation that causes Duchenne muscular dystrophy that CRD is currently working to treat, meaning they can be utilized for critical in vivo studies to test the safety and efficacy of mutation-specific gene editing therapeutics. The success of this project paves the way for future therapeutics to be developed to treat rare and ultra-rare genetic disorders.
In the media, people with disabilities often aren’t featured as main characters, if they are included at all, so we wanted to share some kid-friendly shows and movies to help teach kids about acceptance and inclusion. Representation in movies and TV shows is important because it shows people, especially younger kids, that not everyone will look or act the same way and that it is important to be accepting no matter what.