Blog

Hear community perspectives on topics ranging from navigating a diagnosis to reflecting on clinical trial experiences.

September 26, 2025
Cure Rare Disease Secures FDA Orphan Drug Designation for Investigational Gene Therapy to Treat Limb-Girdle Muscular Dystrophy Type R9 (LGMD2i/R9)

Designation supports development of CRD-003, an investigational therapy targeting the root cause of Limb-Girdle Muscular Dystrophy Type R9

POPULAR
Anatomy of A Gene

Testing CRISPR Therapeutics in DMD Patient Cells: Process and Timeline

SCA3 Program Overview

CRD Patient Registry: How to Join

30 With DMD: Finding My Life’s Purpose

I’m Vivek Gohil, I’m 30, and I live with Duchenne Muscular Dystrophy. My life goal is to leave a mark, make the most of life, and help others along the way. Although it’s daunting, I never worry about the future.…

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