Cure Rare Disease: Changing the Paradigm to End Duchenne & Rare Disease
We bridge the gap between researchers and a cure through an unprecedented customized medicine development, by supporting families through their journey and educating the global community.
Our collaborations strive to accelerate cures for rare genetic disorders including but not limited to Muscular dystrophies (Duchenne, Limb-girdle, Becker’s), Charcot-Marie-Tooth, cystic fibrosis, Sickle Cell disease, Canavan disease and Spinal Muscular Atrophy.
Power in Community Conference
Sunday, July 21, 2019
Museum of Science – Boston, MA
Cure Rare Disease hosted its annual Power in Community Conference 2019 to provide a platform for Duchenne/Becker’s muscular dystrophy families, clinicians and drug developers to ask questions and connect. The conference provided each group the opportunity to better understand the needs and progress of ground-breaking therapies under development and evolving standards of care.