We previously lived in Central California and raised organically fed pork on pasture. When Kal was diagnosed with Duchenne...

CRISPR mediated exon-skipping is a method of genome editing that can be used to develop life-saving therapeutics for people with rare and ultra-rare genetic disorders. CRD is explaining the science behind these technologies as well as how they are the key to treating these diseases.

Cure Rare Disease, in partnership with Charles River Laboratories, has successfully created 3 mouse models that harbor the humanized form of the dystrophin gene. Each model has a mutation that causes Duchenne muscular dystrophy that CRD is currently working to treat, meaning they can be utilized for critical in vivo studies to test the safety and efficacy of mutation-specific gene editing therapeutics. The success of this project paves the way for future therapeutics to be developed to treat rare and ultra-rare genetic disorders.

It's National Disability Awareness Month, and what better way to celebrate than by highlighting some amazing TikTok creators who share their stories and journeys of living with a disability.

In the media, people with disabilities often aren’t featured as main characters, if they are included at all, so we wanted to share some kid-friendly shows and movies to help teach kids about acceptance and inclusion. Representation in movies and TV shows is important because it shows people, especially younger kids, that not everyone will look or act the same way and that it is important to be accepting no matter what.