Revolutionizing Ultra-Rare Disease Treatment through Innovation and Collaboration

Revolutionizing Ultra-Rare Disease Treatment through Innovation and Collaboration

What We're Working Towards

By Rich Horgan, Founder & CEO, Cure Rare Disease

We envision a future where every patient has access to treatment. Through the CRD drug development model, we aim to increase the efficiency of developing treatments for neglected diseases, ensuring that patients have access to the hope of a healthier future.

Ultra-rare disease is a hidden epidemic.

01

1 in 10

people are diagnosed with a rare disease. The majority affected are children.

02

7,000+

rare-diseases and counting. Most are life-threatening.

03

95%

of all rare diseases currently have no treatment or cure.

Ultra-rare disease is a hidden epidemic.

In the U.S. and Canada alone, 37 million people have a rare disease.

01

1 in 10

people are diagnosed with a rare disease.
The majority affected are children.
02

7000+

rare diseases and counting.
Most are life-threatening.
03

95%

of all rare diseases currently have
no treatment or cure.

Our Process

Our model aims to streamline and de-risk the development of therapies for ultra-rare diseases.

Our model aims to streamline and de-risk the development of therapies for ultra-rare diseases

PHASE 1

Research & Development

CRD selects a disease and identifies academic research collaborators. We establish a research agreement to enable early stage development.

THE CRD ECOSYSTEM

CRD is a builder, streamlining a fragmented system.

CRD is a drug development engine, bringing together early stage research with CRD’s drug development expertise.

Partner With Us
Cure Rare Disease

Academic Research

Provide early stage drug design and development expertise 

Patient
Families

Provide treatments to neglected, ultra-rare disease patients

Rare Disease Organizations

Provide information and support to families and community groups

Biotech & Pharma

Provide de-risked pipeline of new technologies

CRD IN THE NEWS

Support our work.

Your involvement helps shape our research and ensures our therapies meet real patient needs.