Your donation helps Cure Rare Disease’s continuous efforts to advance research to treat rare, genetic diseases. Thank You!
Please consider making a small, monthly donation to support the work of Cure Rare Disease. Every donation helps us advance closer to a cure! Donations made now will go to support our dose-range finding study which will help us understand the optimal amount of the therapeutic to give.
The experience of rare disease can be overwhelming for both patients and their families. Diagnoses are often difficult, involving repeated visits to multiple specialists. Once a diagnosis is made, patients live with severe restrictions and life expectations, not to mention the tumult of having hopes raised and then dashed through successive treatments.
To overcome the obstacles inherent in the existing model of drug development, CRD has take a new approach. Rather than awarding grants to independent investigators, the organization has formed an unprecedented collaboration with leading researchers in genetics, genomics and biotechnology, bioinformatics and customized therapy development.
In a short period of time, CRD has achieved significant milestones and breakthroughs to advance our efforts. We are engaging a number of entrepreneurs, venture capitalists, philanthropists and scientists who share our vision for a more effective model to treat rare, genetic diseases. With significant successes, we are poised to realize the vision of customized therapeutics within a short period of time.